Han Phan, MD

Title: Director

Organization: Rare Disease Research, LLC

Bio: Dr. Han Phan is a pediatric neurologist and sleep specialist who is highly passionate about clinical trials in neuromuscular diseases, specifically Duchenne Muscular Dystrophy and Spinal Muscular Atrophy. She is a member of the Pediatric Advisory Board at the FDA and a guest researcher at the CDC Newborn Screening Branch. She is currently an Associate Professor at the University of Alabama, and codirector of MDA clinic. At Rare Disease Research center, she is the principal investigator overseeing ongoing studies in neuromuscular patients.

Beyond Dystrophin Panel

This conference session provides insight and updates from companies whose therapies target critical aspects of the Duchenne disease process that occur alongside reductions in dystrophin.

Abby Bronson

Vice President, Patient Advocacy & External Innovation

Edgewise Therapeutics

Mindy Cameron

Patient Advocacy Lead

Santhera Pharmaceuticals

Matthew Klein, M.D., M.S., FACS

Chief Operating Officer

PTC Therapeutics

Daniel Paulson, MD

Vice President of Clinical Development

Capricor Therapeutics

Han Phan, MD


Rare Disease Research, LLC