The table below contains those trials currently enrolling Duchenne patients and involving active drugs, as of the date indicated.

A more complete listing of Duchenne trials may be found at ClinicalTrials.gov.

RESEARCH COMPANY COMPOUND STATUS INDICATION LOCATION CLINICAL TRIAL
Anti-fibrotic, Anti-Inflammatory, Regenerative Agent Italfarmaco Givinostat Phase 3 Males with Duchenne 6-17 years old US, EU, CA, UK VIEW DETAILS
Anti-inflammatory Mallinckrodt MNK-1411 Cosyntropin Phase 2 Males with Duchenne 4-8 years old United States VIEW DETAILS
ReveraGen BioPharma Vamorolone / Prednisone Phase 2b Males with Duchenne 4-7 years old CO, FL, NC, PA, VA, WA VIEW DETAILS
Anti-inflammatory / Muscle Regeneration Capricor Cap-1002 Phase 2 Males with Duchenne 10 years and older CA, CO, FL, MO, OH, UT VIEW DETAILS
Exon Skipping Sarepta Eteplirsen Phase 2 Males with Duchenne ages 6 to 48 months UK, EU VIEW DETAILS
Sarepta SRP4045 SRP4053 Phase 3 Males with Duchenne ages 7-13 US, EU, CA, IL, UK VIEW DETAILS
Sarepta SRP-5051 Phase 1 Males with Duchenne ages 12 years and older US VIEW DETAILS
Wave WVE-210201 Phase 1 Ages 5 to 18, amenable to exon 51 skipping, ambulatory and non-ambulatory boys US, FR, UK VIEW DETAILS
Gene therapy Nationwide Children’s Hospital GALGT2 Phase 1/2 Males with Duchenne 4 years and older Ohio VIEW DETAILS
Nationwide Children’s Hospital Microdystrophin Phase 1/2a Males with Duchenne 3 mos to 3 years and 4 to 7 years Ohio and Missouri VIEW DETAILS
Pfizer PF 06939926 Phase 1 Males with Duchenne 5-12 years old US VIEW DETAILS
Solid GT SGT-001 Microdystrophin Phase 1/2 Males with Duchenne 4-17 years old Florida VIEW DETAILS
Membrane Sealant Phrixus Pharmaceuticals P-188 NF (Carmeseal-MD™) Phase 1 Males with Duchenne 12-25 years old Ohio VIEW DETAILS
Mitochondrial Function Cardero (+)Epicatechin Phase 1/2 Males with Duchenne 8-17 years old UC Davis VIEW DETAILS
Santhera Idebenone Phase 3
SIDEROS Trial
Males with Duchenne 10 years and older US, EU, UK, IL, IE VIEW DETAILS
Muscle Regeneration Roche BMS-986089 Phase 2/3 Males with Duchenne 6-11 years old US, EU, UK, JP, AR, AU, CA VIEW DETAILS
Stop Codon readthrough PTC Ataluren Phase 3 Males with Duchenne 5 Years and older US, AU, HK, JP, IN, KR, MY, RU, TW VIEW DETAILS

Chart updated on 9/12/18