Pinkies Up To Cure Duchenne

Click below to learn how to participate

1st

Drug approved by the FDA
for the treatment of Duchenne.
CureDuchenne was an early funder.

12

CureDuchenne funded research projects
have advanced to human clinical trials

Give them a fighting chance

Learn more about Duchenne

BE A MEMBER OF OUR PATIENT REGISTRY

Enroll here to make sure you’re alerted and aware of the latest pharmaceutical treatments for Duchenne muscular dystrophy that become available as research progresses every day.

Our lives were changed forever…

“We didn’t know anything about Duchenne and felt isolated that there was no one we could turn to… CureDuchenne has hosted several workshops that have been invaluable in providing knowledge on the care, treatment and future of our son, but, even more importantly, has enabled us to spend time with other Duchenne families…”

READ FAMILY STORY

Duchenne is a devastating muscle disease.

It’s the most common and severe form of muscular dystrophy. Those affected with Duchenne lose their ability to walk, feed themselves, breathe independently and succumb to heart failure. But there’s hope through new pharmacological and gene-based therapies. You can help make a difference.

LEARN ABOUT THE DISEASE

UPCOMING EVENTS, WORKSHOPS & WEBINARS

03 November @ 08:00 am - 05:00 pm

CureDuchenne Futures

Join us for 2 days of insightful discussion about the future of Duchenne muscular dystrophy. Click here for more info. Click here to Register.

10 November @ 07:00 am - 10:00 pm

Napa in New England

Join us for an Extraordinary Evening Benefiting CureDuchenne Wine connoisseurs and epicureans across New England can now experience some of the finest wines from California’s Napa Valley, right in our own backyard.  Cult wine brands, exquisite cuisine and unparalleled auction lots featured at Napa in New England will transport you to a world that unites […]

CureDuchenne Futures

Join us for 2 days of insightful discussion about the future of Duchenne muscular dystrophy. Click here for more info. Click here to Register.

08:00 am - 05:00 pm
100 Cabot St
27September
Learn More

DUCHENNE ARTICLES

NEWPORT BEACH, Calif. – (BUSINESS WIRE) – CureDuchenne, a national venture philanthropy nonprofit focused on finding a cure for Duchenne muscular dystrophy (DMD), announced today a $500,000 investment into 4D Molecular Therapeutics (4DMT), a world-leader in Therapeutic Vector Evolution for adeno-associated virus (AAV) gene therapy vector discovery and product development, in an effort to advance […]

CURE DUCHENNE NEWS

Investment advances pre-clinical development of novel exon skipping therapies for treatment of patients with Duchenne muscular dystrophy October 17, 2018 08:00 AM Eastern Daylight Time LA JOLLA, Calif.–(BUSINESS WIRE)–Avidity Biosciences, a privately held biotech company pioneering a new class of precision medicines based upon antibody-oligonucleotide conjugates, announced today that CureDuchenne has made an equity investment […]

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