1st

Drug approved by the FDA
for the treatment of Duchenne.
CureDuchenne was an early funder.

9

CureDuchenne funded research projects
have advanced to human clinical trials

BE A MEMBER OF OUR PATIENT REGISTRY

Enroll here to make sure you’re alerted and aware of the latest pharmaceutical treatments for Duchenne muscular dystrophy that become available as research progresses every day.

Our lives were changed forever…

“We didn’t know anything about Duchenne and felt isolated that there was no one we could turn to… CureDuchenne has hosted several workshops that have been invaluable in providing knowledge on the care, treatment and future of our son, but, even more importantly, has enabled us to spend time with other Duchenne families…”

READ FAMILY STORY

Duchenne is a devastating muscle disease.

It’s the most common and severe form of muscular dystrophy. Those affected with Duchenne lose their ability to walk, feed themselves, breath independently and succumb to heart failure. But there’s hope through new pharmacological and gene-based therapies. You can help make a difference.

LEARN ABOUT THE DISEASE

UPCOMING EVENTS, WORKSHOPS & WEBINARS

15July
15 July @ 04:00 am - 10:30 pm

AlaskaMack Extreme Swim, Bike, and Run to CureDuchenne

David is competing in the AlaskaMan(TM) in supporting the effort to find a cure for Duchenne.

27July
27 July @ 06:00 am - 11:00 pm

Jim’s Gaelic Touras 2017

Jim Ruetz will be hitting the road for his 4th time to raise awareness and money for research for Duchenne muscular dystrophy. Jim’s Gaelic Touras will take him through Ireland and Scotland this summer.

08September
08 September @ 05:30 pm - 09:00 pm

7th Annual Getzlaf Golf Shootout

The 7th Annual Getzlaf Golf Shootout – hosted by Ryan Getzlaf, captain of the Anaheim Ducks – is a two-day charity golf event that brings together athletes, celebrities and community leaders.

04October
04 October @ 08:30 am - 04:30 pm

Duchenne: Current Understanding and Treatment – Los Angeles, CA

This course is ideal for physical therapists, occupational therapists, speech language pathologists, and others involved in the care of persons with Duchenne.

1 2

7th Annual Getzlaf Golf Shootout

The 7th Annual Getzlaf Golf Shootout – hosted by Ryan Getzlaf, captain of the Anaheim Ducks – is a two-day charity golf event that brings together athletes, celebrities and community leaders.

05:30 pm - 09:00 pm
08September
Learn More

DUCHENNE ARTICLES

Liestal, Switzerland, June 22, 2017 – Santhera Pharmaceuticals (SIX: SANN) announces that the UK`s Medicines and Healthcare products Regulatory Agency (MHRA) has granted Raxone (idebenone) a positive scientific opinion through the Early Access to Medicines Scheme (EAMS) for patients with respiratory function decline not taking glucocorticoids in Duchenne Muscular Dystrophy (DMD). The aim of the EAMS is […]

CURE DUCHENNE NEWS

NEWPORT BEACH, Calif., June 15, 2017 – RASRx announced today that the United States Food and Drug Administration (FDA) has granted an Orphan Drug Designation (ODD) for its compound RASRx1902 for the treatment of Duchenne Muscular Dystrophy.  RASRx1902 is an oral therapy that has shown positive effects on muscle function in animal models of Duchenne.  […]

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