Our mission is to save this generation of children and young adults with Duchenne muscular dystrophy.
CureDuchenne is recognized as the global leader in research, patient care and innovation for improving and extending the lives of those with Duchenne.
We operate with integrity through compassion, and empowering the community nationally with positive solutions.
Our actions fuel hope for families, enable progress for drug development, and extend ambulation for patients in collaboration with pharmaceutical companies, medical and healthcare professionals, our scientific advisory board, and our board of directors.
CURE, CARE, COMMUNITY
Accelerating the Cure, Redefining Care, Building Community
The funds we raise support the most promising research programs aimed at treating and curing the disease. We have also garnered international attention for our efforts to raise funds and awareness through venture philanthropy (CureDuchenne Ventures). For the first time, there is hope for this destructive disease affecting thousands of children and their families.
CureDuchenne has leveraged more than $2.3 billion in follow-on investment from venture capital, biotech, and pharmaceutical companies to fund research. To date, nine CureDuchenne research projects have advanced into human clinical trials. That’s a unique accomplishment. And we contributed funding to Sarepta Therapeutics, the first company to have an FDA-approved drug for Duchenne.
Under our CureDuchenne Cares banner, we strive to increase the health and wellbeing of patients living with Duchenne through educating parents, caregivers, clinicians and physical therapists on best practices. Our goals are to improve outcomes, extend ambulation, and offer guidance on disease management and care.
This program also keeps families informed on the latest scientific developments in Duchenne research, including status and participation in clinical trials. We provide workshops and webinars on a wide range of topics. And we’ve created the CureDuchenne Cares Certified Physical Therapist program to ensure high standards of care. In short, we strive to build a community where all parties involved can share information, get the resources they need and find mutual support.