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Will you help us Cure Duchenne now?
My son, Justin Paul Monastesse, was a gift and he lived with Duchenne for more than 25 years. Justin always had a great time even though it took 2 1/2 […]
Current Status of Drisapersen Studies: analyses and assessment of next steps are ongoing
Dear Patient Group Representative, On the 20th of September this year, we shared the results about our Phase III study (DMD114044) of drisapersen in boys with Duchenne Muscular Dystrophy […]
Exon Skipping as a Potential Treatment for Duplication Mutations in Duchenne
Click here for the recorded webinar: https://cc.readytalk.com/cc/playback/Playback.do?id=2lyea5 CureDuchenne has been an early and important funder of exon skipping research for Duchenne. As we gain visibility to an actual therapeutic with exon […]
Summary of the DIA and NORD Conference
The “U.S. Conference on Rare Diseases & Orphan Products: The New Era in Health Care” hosted by DIA and the National Organization for Rare Disorders (NORD) was held in Bethesda, […]
Highlights from the Sarepta Webinar Regarding Etiplersen and Additional Exon Skipping Programs for Duichenne Muscular Dystrophy.
This is a very brief summary of some of the key points from this morning’s webinar hosted by Sarepta and moderated by Chris Garabedian, CEO and Ed Kaye, CMO. CureDuchenne […]
Recap of GSK and Prosensa October 15 Webinar
On Tuesday October 15, GSK and Prosensa conducted a conference call for the Duchenne community, especially for members that may not have been at several of the recent meetings where […]
GSK and Prosensa will hold a joint webinar on Tuesday, October 15, 2013 at 11 a.m. ET and 8 a.m. PT
Dear Patient Group Representative, GSK and Prosensa will hold a joint webinar on Tuesday 15th October 2013 at 4:00 PM British Summer Time (GMT+0100) for the DMD patient community. […]
GSK/Prosensa Duchenne Community
Dear Patient Group Representative, GSK and Prosensa will hold a joint webinar on Tuesday 15th October 2013 at 8:00 am Pacific, 11:00 am Eastern for the DMD patient community. Pre-registration entry for […]
Sarepta Therapeutics to Host Webcast and Conference Call for Duchenne Muscular Dystrophy Community on October 17
We wanted to let you know that Sarepta Therapeutics will host a webcast and conference call on October 17. Please see information below from Sarepta. We encourage you to submit […]