Sibling Saturday: Finding Inspiration in All Shapes and Sizes
No matter how long we live, the ones who will have known us the longest are our siblings. For siblings Wil and Emily Cook, the time they have together is […]
No matter how long we live, the ones who will have known us the longest are our siblings. For siblings Wil and Emily Cook, the time they have together is […]
PTC Therapeutics held a community conference today regarding Ataluren. Stuart Peltz, President and CEO, PTC Therapeutics, Inc., welcomed and thanked the community as well as […]
Dear Duchenne Community, As you might have seen, the Office of Drug Evaluation I of the FDA provided a Complete Response Letter (CRL) for the application to market ataluren in […]
PTC Therapeutics received a Complete Response Letter from the Food and Drug Administration (FDA) for Ataluren’s New Drug Application (NDA). This means that the FDA has completed its review of […]
The 22nd International Annual Congress of the World Muscle Society took place in St Malo, between October 3 – 7, 2017. There were multiple breaking news stories on Duchenne muscular […]
Dear Duchenne Community, On behalf of all of PTC, we want to thank all of you for supporting the advisory committee review of ataluren. As you know, the meeting was […]
Leading a healthy lifestyle is something that any individual should aim towards. For those with Duchenne, making nutritional modifications has the potential to improve their overall health. Research has indicated […]
CureDuchenne firmly believes in working together to help any child with Duchenne muscular dystrophy find the support they need. Duchenne is a disorder which knows no cultural, economic, or social […]
Today, Dr. Eric Olson spoke at the UT Southwestern Wellstone Muscular Dystrophy Center Duchenne Muscular Dystrophy Clinical Symposium. He presented promising pre-clinical data about gene editing using CRISPR/Cas9 for Duchenne. […]