Help Advance Research to Treat Heart Disease
CureDuchenne Ventures LLC is investing $1 million in Capricor Therapeutics to advance promising research to treat disease associated with Duchenne muscular dystrophy.
Join a CureDuchenne event
CureDuchenne has a variety of fundraising events throughout the year. These events have helped us fund seven research projects that have gone to human clinical trials. Join us for CureDuchenne's Paddle Battle LA on June 27th 2015 in Los Angeles, CA.
Duplication Mutation Therapy for Duchenne
CureDuchenne has provided the lead funding for Dr. Flanigan's duplication research and is committed to helping bring this therapy into trials. We need your support in raising $710,000 to continue this important research.
Moving research into practice
CureDuchenne’s accelerated push to move research from the lab into clinical trials could halt the progression of the disease and save the lives of thousands of Duchenne boys.
Accelerating access to Duchenne drug candidates
CureDuchenne is now funding $7 million Prosensa exon skipping research to help get experimental medicines to patients with Duchenne Muscular Dystrophy more quickly.
Together, we can CureDuchenne
Duchenne muscular dystrophy is a devastating muscle disease in children, affecting one in every 3,500 male births. Historically, Duchenne boys have not lived beyond their mid-20s. Those that do are faced with progressively weaker muscles and pulmonary and cardiac failure. The potential now exists, however, to make a difference in their quality of life.
What is CureDuchenne?
CureDuchenne is a national nonprofit that raises awareness and funds to find a cure for Duchenne muscular dystrophy. The funds we raise support the most promising research programs aimed at treating and curing the disease. For the first time ever there is hope to find a cure for this destructive disease affecting thousands of boys and their families.
Sign up for our newsletter
Exon skipping drugs will be used to transform Duchenne muscular dystrophy into a much milder disease as seen in Becker muscular dystrophy patients. eDystrophin is an online database that provides information about inframe mutations typically seen in patients with milder forms of the disease. The database has been constructed using patient records and is easy to use and searchable by mutation type or clinical phenotype.
The Latest from the Founder
The PJ Nicholoff Steroid Protocol April 23, 2015
CureDuchenne Cares is pleased to share important information about steroids use for Duchenne patients. Use of corticosteroids is part of the standards of care for Duchenne patients. Chronic use of steroids is accompanied by side effects, but rapid withdrawal of steroids can lead to serious, life threatening conditions as well. This was exemplified in Read more »Continue reading