Part 1 of the series engages families who have recently begun their Duchenne journey, or those who could benefit from introductory-level presentations on the following topics: Message From A Duchenne […]
CureDuchenne cornered the best and brightest to gather relevant information for people living with Duchenne. Tiffany Cook asks the questions you’ve been thinking – from experts in their field who […]
Descripción: Un evento virtual de dos horas centrado en la información sobre COVID-19 y los recursos en el hogar para las personas que viven con Duchenne. Seminario web de Zoom: Abierto al público, dirigido a la comunidad de Duchenne de habla hispana Panelistas: Dr. […]
In this webinar, moderated by Tiffany Cook, MS, CCC-SLP, Senior Director of CureDuchenne Cares, the mental health presentation by Paige Lembeck, PhD, will be followed by several presentations from biopharmaceutical companies […]
In this webinar, Beth Belluscio, MD, PhD, Pfizer Global Clinical Lead for Rare Neurological Disorders, discusses the Phase 3 study of PF-06939926, a gene therapy for Duchenne muscular dystrophy. Dr. Belluscio answers questions […]
In this webinar, Sarepta Therapeutics discusses their patient support program, SareptAssist, intended to support individuals through the process of starting and staying on commercial therapy. Services provided by SareptAssist include […]
Suvodirsen (formerly known as WVE-210201) is an investigational stereopure oligonucleotide being developed as a potential treatment for boys with Duchenne muscular dystrophy with mutations amenable to exon 51 skipping. Wave […]
We will provide an update on the scientific rationale for use of vamorolone, and share some results from our open-label Long Term Extension study. The very important pivotal clinical trial […]
