Ask the Experts Video Series Webinars

CureDuchenne cornered the best and brightest to gather relevant information for people living with Duchenne.   Tiffany Cook asks the questions you’ve been thinking – from experts in their field who […]


Información y recursos de Duchenne sobre COVID-19 

Descripción: Un evento virtual de dos horas centrado en la información sobre COVID-19 y los recursos en el hogar para las personas que viven con Duchenne. Seminario web de Zoom: Abierto al público, dirigido a la comunidad de Duchenne de habla hispana Panelistas: Dr. […]


Pfizer’s Phase 3 Study of Gene Therapy for DMD

In this webinar, Beth Belluscio, MD, PhD, Pfizer Global Clinical Lead for Rare Neurological Disorders, discusses the Phase 3 study of PF-06939926, a gene therapy for Duchenne muscular dystrophy. Dr. Belluscio answers questions […]

Webinar Sarepta

Sarepta Patient Support Program Webinar

In this webinar, Sarepta Therapeutics discusses their patient support program, SareptAssist, intended to support individuals through the process of starting and staying on commercial therapy. Services provided by SareptAssist include […]

Webinar Vamorolone

Update on the Vamorolone Program

We will provide an update on the scientific rationale for use of vamorolone, and share some results from our open-label Long Term Extension study. The very important pivotal clinical trial […]

Duchenne Clinical Trials & Drug Development

In rare diseases such as Duchenne, where the disease population is small, the drug development process can vary from that of more common diseases, and totally new treatment approaches such […]