Today we announced that the U.S. Food and Drug Administration has placed our Phase I/II clinical trial for SGT-001, IGNITE DMD, on Clinical Hold following a serious adverse event that occurred in the first patient dosed, a non-ambulatory adolescent. The patient was admitted to the hospital, received treatment and, as of the writing of this letter, is home with his family with no symptoms. Details about the event can be found in the press release we issued today, which is available here. The team at Solid will be working with the principal investigator and FDA to fully understand the cause and nature of this event, as well as identify appropriate next steps as soon as possible.
Dr. Wagner and the CureDuchenne team provided information about Santhera Pharmaceuticals' expanded access and compassionate use in the U.S., the BreatheDMD program, and Santhera answered questions from the community.
NEWPORT BEACH, Calif., Feb. 2, 2018 /PRNewswire/ — CureDuchenne, a nonprofit that funds research to find a cure for Duchenne muscular dystrophy, pioneered the community-based CureDuchenne Cares program which provides families, caregivers, and individuals living with Duchenne an interactive education and supportive program. With support from biotech and pharmaceutical companies, CureDuchenne Cares brings to local communities critical resources that can positively […]
Matches Donations to Fund Duchenne Research NEWPORT BEACH, CA (December 2, 2017) – In Week 13 of the NFL season, Clay Matthews of the Green Bay Packers will take to the field with his heart on his feet. This year, the NFL is continuing its ‘My Cause My Cleats’ campaign where NFL players design cleats […]
Join CureDuchenne’s Celebrated Event on March 3, 2018, at the Ritz-Carlton, Laguna Niguel NEWPORT BEACH Calif., November 15, 2017 – For those who appreciate the earthen opulence of wine country, exquisite cuisine and unparalleled auction lots, Southern California’s premier wine event is back for the much-anticipated 4th Annual Napa in Newport Wine Auction, to be […]
Philadelphia, PA (October 31, 2017) – Philadelphia celebrities and more than 250 prominent leaders, community members and guests raised $240,000 to fund Duchenne muscular dystrophy research at the fourth annual BLINGO to CureDuchenne on October 14 at The Westin Philadelphia. This binged-out evening presented by Cross Properties, benefited CureDuchenne, a national nonprofit that raises awareness […]
NEWPORT BEACH, Calif., October 26, 2017 – CureDuchenne, a nonprofit dedicated to funding research and improving patient care for Duchenne muscular dystrophy, launched the CureDuchenne Cares Virtual Durable Medical Equipment (DME) Expo as a resource for the Duchenne community. Mobility equipment is important for those with Duchenne as they start to lose ambulation and muscle […]
Philadelphia celebrities, prominent leaders and community members to gather for a blinged-out evening benefitting the fight against Duchenne Muscular Dystrophy Philadelphia, PA (October 4, 2017) – CureDuchenne, a national nonprofit that raises awareness and funds research to find a cure for Duchenne muscular dystrophy, will put the bling in bingo for their fourth annual fundraiser […]
San Antonio, Texas, October 3, 2017 – Dealing for Duchenne, a charity event to raise funds for research for children afflicted with Duchenne muscular dystrophy, returns to San Antonio on Saturday, October 21. The event will be held at Pedrotti’s North Wind Ranch in Helotes starting at 6 p.m. and will feature casino games, food, […]
— Anaheim Ducks Captain Ryan Getzlaf and Wife Paige Getzlaf Continue their Support of CureDuchenne – Newport Beach, CA (Sept. 20, 2017) – The 7th Annual Getzlaf Golf Shootout benefiting CureDuchenne raised more than $546,000 to help find a cure for Duchenne muscular dystrophy. Hosted by Anaheim Ducks Captain Ryan Getzlaf and his wife Paige, […]