Department of Defense Duchenne Muscular Dystrophy Research Program
July 13, 2011
Liestal, Switzerland, August 24, 2011 - Santhera Pharmaceuticals (SIX: SANN) announced today that the United States Patent and Trademark Office granted patent protection for the use of idebenone (brand name CatenaÂ®) in the treatment of Duchenne Muscular Dystrophy and other muscular dystrophies. The patent in the United States is supplemented by a similar patent in the European Union granted in 2010.
A Clinical Study to Assess the Efficacy and Safety of GSK2402968 in Subjects With Duchenne Muscular Dystrophy (DMD114044)
The purpose of this study is to determine whether GSK2402968 is effective in the treatment of ambulant boys with Duchenne muscular dystrophy resulting from a mutation thought to be corrected by exon 51 skipping.
New compound brings hope of muscular dystrophy remedy
A discovery that strengthens the bodyâ€™s ability to repair muscle tissue could lead to new treatments for people with muscular dystrophy and other degenerative muscle diseases.
Duchenne Muscular Dystrophy Is Ultimately a Stem Cell Disease, Researchers
For years, scientists have tried to understand why children with Duchenne muscular dystrophy experience severe muscle wasting and eventual death.
miRNAs as serum biomarkers for Duchenne muscular dystrophy
February 21, 2011
Dystrophin absence in Duchenne muscular dystrophy (DMD) causes severe muscle degeneration. We describe that, as consequence of fibre damage, specific muscle-miRNAs are released into the bloodstream of DMD patients and their levels correlate with the severity of the disease.