CureDuchenne Blog

BACK TO SCHOOL: Communicating with the Team

Guest blog by Celeste Graham, PT, ex-Director of Physical Therapy, CureDuchenne CaresUPDATED 8/12/2022 We are at that time of year when the shelves of our local superstores that just recently […]

Navigating College, Living with Duchenne

  Guest blog by Hawken Miller For those with Duchenne Muscular Dystrophy the experience and education of a four-year university is likely within your grasp, and being away from home […]

Thoughts about PTC

The announcement that PTC recently submitted an appeal to elevate the “Refusal to File” of Translarna (also known as ataluren and PTC124) to the next level of FDA management is […]

Summer Road Trip

  Guest blog by Hawken Miller Many of the things I don’t think are possible for me to do really are. Once I get over my initial apprehension and thoughts […]

An Update for the Duchenne Community

  We are sharing the following update from Sarepta Therapeutics.   Sarepta Therapeutics is updating the Duchenne community regarding recent changes to the Phase III confirmatory clinical study, ESSENCE (Study […]