Three Things You Missed From the AGAMREE (Vamorolone) Webinar
Agamree (vamorolone) was recently approved by the FDA, and Catalyst explains the new steroid and how to get it in this CureDuchenne Webinar.
Agamree (vamorolone) was recently approved by the FDA, and Catalyst explains the new steroid and how to get it in this CureDuchenne Webinar.
Books are a gateway for us to unlock our imaginations. To see ourselves in the characters that captivate our attention. To let our mind wander to places that wouldn’t have […]
Read Astellas community letter below:
Solid Biosciences Announces IND Clearance by FDA for Duchenne Muscular Dystrophy Gene Therapy Candidate SGT-003
Mother of two boys with Duchenne shares how she’s successfully advocated for her children with a rare disease as a mama bear.
Shopping for someone with a physical disability can seem difficult as this holiday season rolls around. They may not have the same strength or dexterity as other kids and/or adults […]
The silver screen has been featuring more and more stories about people with disabilities, whether it be developmental, physical, or mental. With more representation in popular culture, comes more understanding […]
Sarepta Therapeutics announced topline results from EMBARK
The U.S. FDA announced today its decision to approve AGAMREE (vamorolone), a new steroid for individuals with Duchenne muscular dystrophy 2 years or older. This approval comes largely based on […]