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Letter to Duchenne Community from PTC Therapeutics
We are happy to share the following letter to the Duchenne Community from Stu Peltz, CEO PTC Therapeutics. March 24, 2017 Dear Duchenne Community, We were very excited to […]
A Rare Disease, The Duchenne Story Spreads Because of You
If you told someone your child had cancer, they would immediately have a sense of the disease and potentially even a sense of the treatment options. People know about chemo, […]
Physical Therapist Haydee Bustos is a Pillar of Strength in the Duchenne Community
Haydee Bustos has a passion for helping kids, and through her experience as a physical therapist, she discovered an even deeper desire to help kids with Duchenne muscular dystrophy. […]
An Open Letter to the Duchenne Community
CureDuchenne is sharing an expanded and updated open letter to the Duchenne community from Marathon Pharmaceuticals. An Open Letter to the Duchenne Community Dear Members of the Duchenne Community: […]
An Open Letter to the Duchenne Community
CureDuchenne is sharing an expanded and updated open letter to the Duchenne community from Marathon Pharmaceuticals. An Open Letter to the Duchenne Community Dear Members of the Duchenne Community: […]
FDA Approves EMFLAZA (deflazacort) … Our Experience With Deflazacort
We are delighted that the U.S. Food and Drug Administration (FDA) has approved EMFLAZA (deflazacort) for the treatment of Duchenne. This is wonderful news for the Duchenne community to […]
Additional Information about EMFLAZA (deflazacort) for Duchenne Patients under the Age of Five
Today, the FDA approved the use of EMFLAZA (deflazacort) for Duchenne patients over the age of five years old. It is routine for the FDA to designate specific patient […]
Move DMD Trial Update
The MoveDMD trial with edasalonexent (CAT-1004) in Duchenne muscular dystrophy (DMD) has just completed Part B, and Catabasis has released the top-line results. Summary: The top-line results that […]
Action Alert: Contact Your Texas State Senator Today
Calling all Texans. Take action today and let your voices be heard. Call your Texas State Senator and ask them to support Medicaid funding for the treatment of Duchenne. […]