Scientific Advisory Board 

Barry J. Byrne, M.D., Ph.D.
Professor and Associate Chair of Pediatrics, Molecular Genetics & Microbiology
Director, Powell Gene Therapy Center, University of Florida School of Medicine


 

Kevin Campbell, Ph.D.
Investigator, Howard Hughes Medical Institute Director, Senator Paul D. Wellstone MDCRC, University of Iowa, Carver College of Medicine

 
 

Jeffrey Chamberlain, Ph.D.
Principal Investigator, Chamberlain Lab, Department of Neurology, University of Washington School of Medicine.

  

Cristina Csimma, PharmD, MHP

Chief Executive Officer,

Cydan Development, Inc.

 

 

Eric Hoffman, Ph.D.
Director, Research Center for Genetic Medicine, George Washington School of Medicine and Health Sciences, Children's National Medical Center, Washington DC

 

Edward Michael Kaye, M.D.
Senior Vice President and Chief Medical Officer
Sarepta Therapeutics


Douglas Macdonald, Ph.D.
Director, Drug Discovery
CHDI Management, Inc.


M. Carrie Miceli, Ph.D.
Professor, Department of MIMG, David Geffen School of Medicine at UCLA and UCLA College of Letters and Science

 

Kannebovina Nagaraju, Ph.D.
Associate Professor, Pediatrics Research Center for Genetic Medicine
Children’s National Medical Center

 

Stanley F. Nelson, M.D.
Professor, Department of Human Genetics, David Geffen School of Medicine at UCLA


Pier Lorenzo Puri, M.D., Ph.D.
Associate Professor, Muscle Development Regeneration Program
Sanford-Burnham Medical Research Institute, La Jolla, CA


Thomas A. Rando, M.D., Ph.D.
Professor, Department of Neurology and Neurological Sciences, Stanford University School of Medicine