Table of Contents
THE FACES OF DUCHENNE- June, 2006

  • Fast Tracking Research into Viable Treatments for Our Boys
  • Prosensa Receives Orphan Drug Status
  • Prosensa Granted First Human Trial of Exon Skipping
  • Thinking Outside the Box:  CureDuchenne Helps the Whiz Kids
  • PTC in Phase 2 Trials for Promising Drug Therapy
  • Working Towards the Cure:  Gene Therapy
  • The Problem
  • The Solution
  • CureDuchenne on the Right Track!

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